Bob DeMarco Alzheimer's Reading Room

Wednesday, April 15, 2009

Twins Suffering From Alzheimer's Get FDA Compassionate use Exception


The FDA has granted special permission for two, five year old twins girls, to receive intravenous infusions of 2-Hydroxypropyl-beta-Cyclodextrin (also known as HPBCD). The girls received the go ahead for the treatment after a "compassionate use" exception was granted.

The girls are suffering from Niemann Pick Type C disease, a fatal cholesterol metabolism disorder that is often referred to as the "Childhood Alzheimer’s".

This is a gut wrenching story. If you would like to learn more, or meet Addi and Cassi Hempel, go here.


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Alzheimer's Disease -- Advice and Insight


Bob DeMarco is the Founder of the Alzheimer's Reading Room and an Alzheimer's caregiver. The blog contains more than 2,255 articles with more than 272,100 links on the Internet. Bob resides in Delray Beach, FL.



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